Studies indicate that it is possible to achieve long-term gene transfer into hematopoietic stem cells and progenitor cells. But what needs to be done before we can take the final steps towards human stem cell gene therapy (pages 652–658)?
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Dick, J. Gene therapy turns the corner. Nat Med 6, 624–626 (2000). https://doi.org/10.1038/76188
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DOI: https://doi.org/10.1038/76188
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