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Hematopoietic stem cell transplantation for the treatment of childhood cerebral X-linked adrenoleukodystrophy

Nature Clinical Practice Neurology volume 4, pages 130–131 (2008)Cite this article

boxed-textMahmood A et al. (2007) Survival analysis of haematopoietic cell transplantation for childhood cerebral X-linked adrenoleukodystrophy: a comparison study. Lancet Neurol 6: 687–692

Screening of newborns for X-linked ALD, coupled with careful and regular monitoring for progression to CCALD, will provide the best chance of halting progression to disease by treatment with hematopoietic stem cell transplantation

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Acknowledgements

The synopsis was written by Sarah Price, Assistant Editor, Nature Clinical Practice.

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  1. L Maccotta is a Resident in Neurology at the University of California, San Francisco and EH Sherr is an Assistant Professor in Neurology and Pediatrics, Director of the Brain Development Research Program and Co-director of the University of California, San Francisco Neurometabolic Program and Clinic, San Francisco, CA, USA.,

    Luigi Maccotta & Elliott H Sherr

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  1. Luigi Maccotta
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  2. Elliott H Sherr
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Correspondence to Elliott H Sherr.

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Maccotta, L., Sherr, E. Hematopoietic stem cell transplantation for the treatment of childhood cerebral X-linked adrenoleukodystrophy. Nat Rev Neurol 4, 130–131 (2008). https://doi.org/10.1038/ncpneuro0729

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