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Successful bone marrow transplantation in two sisters with activated phosphoinositide 3-kinase δ syndrome 2

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Acknowledgements

We thank all participating doctors whose comments and suggestions were of inestimable value for the study and clinical practices. This work was supported by grants from Research on Measures for Intractable Diseases; Comprehensive Research on Disability Health and Welfare, the Strategic Research Program for Brain Science; Initiative on Rare and Undiagnosed Diseases in Pediatrics and Initiative on Rare and Undiagnosed Diseases for Adults from the Japan Agency for Medical Research and Development; Grants-in-Aid for Scientific Research on Innovative Areas (Transcription Cycle) from the Ministry of Education, Science, Sports and Culture of Japan; Grants-in-Aid for Scientific Research (B) from the Japan Society for the Promotion of Science; Creation of Innovation Centers for Advanced Interdisciplinary Research Areas Program in the Project for Developing Innovation Systems from the Japan Science and Technology Agency; grants from the Ministry of Health, Labor and Welfare; the Takeda Science Foundation; the Yokohama Foundation for Advancement of Medical Science and the Hayashi Memorial Foundation for Female Natural Scientists.

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Correspondence to M Sugiyama.

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Sugiyama, M., Iguchi, A., Yamada, M. et al. Successful bone marrow transplantation in two sisters with activated phosphoinositide 3-kinase δ syndrome 2. Bone Marrow Transplant 52, 1678–1680 (2017). https://doi.org/10.1038/bmt.2017.189

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